Stable in vivo expression of the cystic fibrosis transmembrane conductance regulator with an adeno-associated virus vector

Terence R. Flotte, Sandra A. Afione, Carol Conrad, Sharon A. McGrath, Rikki Solow, Hidemi Oka, Pamela L. Zeitlin, William B. Guggino, Barrie J. Carter

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419 Scopus citations

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Medicine & Life Sciences