Pharmacokinetics, safety and tolerability of miglustat in the treatment of pediatric patients with GM2 gangliosidosis

Gustavo H.B. Maegawa, Paul L.M. van Giersbergen, Sandra Yang, Brenda Banwell, Christopher P. Morgan, Jasper Dingemanse, Cynthia J. Tifft, Joe T.R. Clarke

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22 Scopus citations

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