Hepatocyte transplantation in a 4-year-old girl with peroxisomal biogenesis disease: Technique, safety, and metabolic follow-up

Etienne M. Sokal, Françoise Smets, Annick Bourgois, Lionel Van Maldergem, Jean Paul Buts, Raymond Reding, Jean Bernard Otte, Veerle Evrard, Dominique Latinne, Marie Françoise Vincent, Anne Moser, Humberto E. Soriano

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216 Scopus citations

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