Genomic safe harbors permit high β-globin transgene expression in thalassemia induced pluripotent stem cells

Eirini P. Papapetrou, Gabsang Lee, Nirav Malani, Manu Setty, Isabelle Riviere, Laxmi M.S. Tirunagari, Kyuichi Kadota, Shoshannah L. Roth, Patricia Giardina, Agnes Viale, Christina Leslie, Frederic D. Bushman, Lorenz Studer, Michel Sadelain