Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia

Dwight D. Koeberl, B. D. Sun, T. V. Damodaran, T. Brown, D. S. Millington, D. K. Benjamin, A. Bird, A. Schneider, S. Hillman, M. Jackson, R. M. Beaty, Y. T. Chen

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