Developing standard procedures for pre-clinical efficacy studies in mouse models of spinal muscular atrophy. Report of the expert workshop "Pre-clinical testing for SMA", Zürich, March 29-30th 2010

Raffaella Willmann, Judith Dubach, Karen Chen, Giorgio Battaglia, Thierry Bordet, Arthur Burghes, Stefania Corti, Christine DiDonato, Bassem El-Khodor, Thomas Gillingwater, Natalie Kayadjanian, Brian Kaspar, Chien Ping Ko, Rudolf Korinthenberg, Rashmi Kothary, George Mentis, Ke Ning, Simon Parson, Marco Passini, Stefanie PossekelJean Marc Raymackers, Daniel Schümperli, Michael Sendtner, Veronica Setola, Charlotte Sumner, Lucia Tabares, Danilo Tiziano, Meg Winberg, Brunhilde Wirth, Rafael Yán˜ez-Mun˜oz

Research output: Contribution to journalArticlepeer-review

16 Scopus citations
Original languageEnglish (US)
Pages (from-to)74-77
Number of pages4
JournalNeuromuscular Disorders
Volume21
Issue number1
DOIs
StatePublished - Jan 1 2011

ASJC Scopus subject areas

  • Pediatrics, Perinatology, and Child Health
  • Neurology
  • Clinical Neurology
  • Genetics(clinical)

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